Cystic Fibrosis and Gene Therapy

How Gene Therapy Plays A Role In This Defect

Cystic Fibrosis - What IS It?

Cystic Fibrosis is an inherited disease of of the secretory glands. The secretory glands are the glands that produce mucus and sweat. People who have CF have to have a gene from both parents. Even if the parents don't exhibit the disease, they can still be carriers of the disease. Cf mainly affects the lungs, pancreas, liver, intestines, sinuses, and sex organs.

Gene Therapy

Gene therapy is a form of therapy that involves inserting one or more correcting genes into the genetic material of a person's cells to cure a genetic disease.Some of the main diseases currently being researched in gene therapy are:
  • Cystic fibrosis
  • Sickle cell anemia
  • Hemophilia
  • Muscular dystrophy
  • Cancer

Gene Therapy and Cystic Fibrosis

Gene therapy offers the best hope for life-saving treatment by tackling the root cause of CF. the basic technique behind gene therapy is identify the defective gene and to correct it with the correct gene which is lab-based.